Hellow guys, Welcome to my website, and you are watching Spinal Muscular Atrophy. and this vIdeo is uploaded by ASGCT at 2019-02-01T01:00:00-08:00. We are pramote this video only for entertainment and educational perpose only. So, I hop you like our website.
| Name | Spinal Muscular Atrophy |
| Video Uploader | Video From ASGCT |
| Upload Date | This Video Uploaded At 01-02-2019 09:00:00 |
| Video Discription | Gene therapy is a fitting approach for diseases caused by a single gene mutation, like SMA. It targets the cause of disease by delivering a fully functioning copy of the gene into motor neuron cells. Let’s learn more about how it works. The subtitling of these videos was funded in part by a donation from Pfizer, Inc. |
| Category | Science & Technology |
| Tags | gene therapy | sma | spinal muscular atrophy | SMN1 | Zolgensma | AVXS-101 | SMA Type 1 | Spinraza | SMN2 | rare disease | pediatrics | child health | science | research |
